Timothy Seabrook1, Laurent Servais2,3, Giovanni Baranello4, John W. Day5, Nicolas Deconinck6, Eugenio Mercuri7, Andrea Klein8, Basil Darras9, Riccardo Masson2,3, Heidemarie Kletzl1, Muna El-Khairi10, Marianne Gerber1, Ksenija Gorni1, Omar Khwaja1
(1.Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, Basel, Switzerland, 2.Institute of Myology, Paris, France, 3.Reference Center for Neuromuscular Disease, Centre Hospitalier Régional de La Citadelle, Liège, Belgium, 4.Carlo Besta Neurological Research Institute Foundation, Developmental Neurology Unit, Milan, Italy, 5.Department of Neurology, Stanford University, Palo Alto, CA, USA, 6.Queen Fabiola Children’s University Hospital, Université Libre de Bruxelles, Brussels, Belgium; Neuromuscular Reference Center UZ Ghent; Ghent, Belgium, 7.Paediatric Neurology and Nemo Center, Catholic University and Policlinico Gemelli, Rome, Italy, 8.University Children’s Hospital Basel, Basel, Switzerland; Inselspital, Bern, Switzerland, 9.Boston Children’s Hospital, Harvard Medical School, Boston, MA, USA, 10.Roche Products Ltd, Welwyn Garden City, UK)
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