AVXS-101 gene-replacement therapy in presymptomatic spinal muscular atrophy（SMA）：study update

Meredith Schultz

[O-168] AVXS-101 gene-replacement therapy in presymptomatic spinal muscular atrophy（SMA）：study update

Meredith Schultz¹, Kathryn Swoboda², Michelle Farrar³, Hugh McMillan⁴, Julie Parsons⁵, Kayoko Saito⁶, Mari Matsuo⁶, Tamaki Kato⁶, Courtney Wells⁷, Francis G. Ogrinc⁷, Bryan E. McGill⁷, Douglas E. Feltner⁷, James LItalien⁷, Douglas M. Sproule⁷, Kevin A. Strauss⁸ (1.University of Wisconsin School of Medicine and Public Health, 2.Massachusetts General Hospital, 3.Department of Neurology, Sydney Childrens Hospital, 4.Childrens Hospital of Eastern Ontario, 5.Childrens Hospital Colorado, 6.Tokyo Womens Medical University, 7.AveXis Inc., 8.Clinic for Special Children)

抄録パスワード認証
パスワードは、「第61回日本小児神経学会学術集会プログラム・抄録集」（「脳と発達」第51巻学術集会号）の『お知らせとお願い』に記載してあります。

講演情報

[O28] 脊髄性筋萎縮症2

[O-168] AVXS-101 gene-replacement therapy in presymptomatic spinal muscular atrophy（SMA）：study update

パスワード