NEURO61

Presentation information

[held on paper]Oral Session

[O-31] Oral Session 31
Clinical trial and Regenerative medicine 1 E

[O-31-1] Long-term Safety and Efficacy of Patisiran in the Global Open-label Extension Study: 24-Month Data

Mitsuharu Ueda1, David Adams2, Alejandra González-duarte3, Elizabeth A Mauricio4, Thomas H Brannagan5, Teresa Coelho6, Jonas Wixner7, Hartmut Schmidt8, Erhan Berber9, Marianne Sweetser9, Matthew T White9, Jing Jing Wang9, Michael Polydefkis10 (1.Department of Neurology, Kumamoto University Hospital, Japan, 2.National Reference Center for FAP (NNERF)/ APHP/ INSERM U 1195/ CHU Bicêtre, Le Kremlin Bicêtre, France, 3.Instituto Nacional de Ciencias Médicas y Nutrición, Salvador Zubirán, Mexico City, Mexico, 4.Mayo Clinic, Jacksonville, FL, USA, 5.Department of Neurology, Columbia University, New York City, NY, USA, 6.Centro Hospitalar Universitário do Porto, Portugal, 7.Department of Public Health and Clinical Medicine, Umeå University, Umeå, Sweden, 8.University Hospital Muenster, Muenster, Germany, 9.Alnylam Pharmaceuticals, Cambridge, USA, 10.Johns Hopkins University, Baltimore, USA)

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