[2S08m] FAONS Symposium
Unlocking Hope : Viral vector-mediated gene therapy for neurological disorders-A promising frontier in therapeutic advancements and future prospects

[2S08m-01] Development and delivery of candidate genome editing therapies for eye and brain diseases

*Paul Thomas^1,2, Ashleigh Geiger^1,2, Stefka Tasheva^1,2, Lachlan Staker^1,2, Jesse Kennedy^1,2, Michaela Scherer^1,2, Sandra Piltz^1,2, Fatwa Adikusuma^1,2 (1. University of Adelaide, Adelaide, Australia, 2. South Australian Health & Medical Research Institute, Adelaide, Australia)

キーワード：genome editing, AAV delivery, genetic blindness , PCDH19 epilepsy