[O-35] 一般演題口演セッション35

[O-35-1] SUNFISH:脊髄性筋萎縮症II型/III型患者でのリスジプラム3年投与の有効性及び安全性

^○齋藤 加代子¹, John W Day², Nicolas Deconinck³, Elena S Mazzone⁴, Andres Nascimento⁵, Maryam Oskoui⁶, Carole Vuillerot⁷, Jessica Braid⁸, Marianne Gerber⁹, Ksenija Gorni⁸, Carmen Martin⁸, Renata S Scalco⁹, Wai Yin Yeung⁸, Eugenio Mercuri⁴ (1.東京女子医科大学,ゲノム診療科, 2.Department of Neurology, Stanford University, Palo Alto, CA, USA, 3.Neuromuscular Reference Center, UZ Gent, Ghent, Belgium, 4.Pediatric Neurology Institute, Catholic University and Nemo Pediatrico, Fondazione Policlinico Gemelli IRCCS, Rome, Italy, 5.Neuromuscular Unit, Neuropaediatrics Department, Hospital Sant Joan de Deu, Fundacion Sant Joan de Deu, CIBERER - ISC III, Barcelona, Spain, 6.Departments of Pediatrics and Neurology Neurosurgery, McGill University, Montreal, Canada, 7.Department of Pediatric Physical Medicine and Rehabilitation, Hopital Mere Enfant, CHU-Lyon, Lyon, France, 8.Roche Products Ltd, Welwyn Garden City, UK, 9.F. Hoffmann-La Roche Ltd, Basel, Switzerland)