[E4] English session
Nerve / Muscular disease

[E-021] FIREFISH Part 1: 1-year event-free survival and swallowing ability in infants with Type 1 SMA

Timothy Seabrook¹, Laurent Servais^2,3, Giovanni Baranello⁴, John W. Day⁵, Nicolas Deconinck⁶, Eugenio Mercuri⁷, Andrea Klein⁸, Basil Darras⁹, Riccardo Masson^2,3, Heidemarie Kletzl¹, Muna El-Khairi¹⁰, Marianne Gerber¹, Ksenija Gorni¹, Omar Khwaja¹ (1.Roche Pharmaceutical Research and Early Development, Roche Innovation Center Basel, Basel, Switzerland, 2.Institute of Myology, Paris, France, 3.Reference Center for Neuromuscular Disease, Centre Hospitalier Régional de La Citadelle, Liège, Belgium, 4.Carlo Besta Neurological Research Institute Foundation, Developmental Neurology Unit, Milan, Italy, 5.Department of Neurology, Stanford University, Palo Alto, CA, USA, 6.Queen Fabiola Children’s University Hospital, Université Libre de Bruxelles, Brussels, Belgium; Neuromuscular Reference Center UZ Ghent; Ghent, Belgium, 7.Paediatric Neurology and Nemo Center, Catholic University and Policlinico Gemelli, Rome, Italy, 8.University Children’s Hospital Basel, Basel, Switzerland; Inselspital, Bern, Switzerland, 9.Boston Children’s Hospital, Harvard Medical School, Boston, MA, USA, 10.Roche Products Ltd, Welwyn Garden City, UK)