[EO-01] Platform Session 01：Neuromuscular Disorders 1

[EO-004] An exon skipping therapy by Viltolarsen on a presymptomatic patient with Duchenne muscular dystrophy

Satomi Ohtaki¹，Nozomi Ryuno¹，Hiromi Teranishi¹，Kaori Sassa¹，Megumi Tsuruoka^2,4，Sayaka Ajihara^1,2，Eri Takeshita³，Yuko Akioka¹，Akira Ohtake^1,2,4，Hirofumi Komaki⁶，Hideo Yamanouchi^1,5 (1. Departments of Pediatrics, Saitama Medical University, Saitama, Japan，2. Departments of Clinical Genomics, Saitama Medical University, Saitama, Japan，3. Department of Child Neurology, National Center Hospital, National Center of Neurology and Psychiatry, Tokyo, Japan，4. Center for Intractable Diseases, Saitama Medical University Hospital, Saitama, Japan.，5. Comprehensive Epilepsy Center, Saitama Medical University Hospital, Saitama, Japan.，6. Translational Medical Center, National Center of Neurology and Psychiatry（NCNP）)