[JO-02] Oral Presentation 02

[JO-010] FIREFISH Parts 1 and 2：Safety and efficacy of risdiplam in Type 1 spinal muscular atrophy

Yasuhiro Takeshima (1. 兵庫医科大学小児科、2. Developmental Neurology Unit、 Fondazione IRCCS Istituto Neurologico Carlo Besta、 Milan、 Italy、3. Department of Developmental Neurology、 Medical University of Gdansk、 Gdansk、 Poland、4. Paediatric Gait Analysis Service of New South Wales、 The Children's Hospital at Westmead、 Sydney、 Austrarila、5. I—Motion—Hopital Armand Trousseau、 Paris、 France、6. Department of Pediatrics、 Peking University First Hospital、 Beijing、 China、7. Department of Neurology、 Faculdade de Medicina、 Universidade de Sao Paulo（FMUSP）、 Sao Paulo、 Brazil、8. Roche Products Ltd、 Welwyn Garden City、 UK、9. F. Hoffmann—La Roche Ltd、 Basel、 Switzerland、10. Department of Neurology、 Boston Children's Hospital、 Harvard Medical School Boston、 MA、 USA)