[P12] 代謝・神経変性疾患

[P12-105] The investigation of 3 cases with SMA type 1 performed different gene therapy courses.

^○Emiko Kobayashi¹, Tomoki Yamauti¹, Sotaro Yuzawa¹, Hiroaki Murakami¹, Tatuya Sakasita¹, Kunihiro Matunami¹, Eiji Matukuma¹, Hideo Kaneko¹, Atushi Imamura¹, Mamoru Yokoyama², Noriko Otuki², Kayoko Saito² (1.Department of Pediatrics, Gifu Prefectural General Medical Cententer,Gifu, Japan, 2.Institute of Medical Genetics Tokyo Women's Medical University)