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[P12-108] オナセムノゲンアベパルボベク治療歴のある脊髄性筋萎縮症小児に対するヌシネルセンの効果：第4相RESPOND試験中間報告

^○本間 泰平¹, Masson Riccardo², Proud Crystal³, Parsons Julie A.⁴, Kuntz Nancy L.⁵, Finkel Richard S.⁶, Richard Foster⁷, Wenjing Li⁸, Bora Youn⁸, Paradis Angela D.⁸, Shweta Rane⁸, Paradis Angela D.¹⁰, Shweta Rane¹⁰ (1.バイオジェン・ジャパン株式会社, 2.Fondazione IRCCS Istituto Neurologico Carlo Besta Milan Italy, 3.Children's Hospital of The King's Daughters, Norfolk, VA, USA, 4.Children's Hospital Colorado, Aurora, CO, USA, 5.Ann and Robert H. Lurie Children’s Hospital of Chicago, Chicago, IL, USA, 6.Children's Hospital of Philadelphia, Philadelphia, PA, USA, 7.Center for Experimental Neurotherapeutics, St. Jude Children's Research Hospital, Memphis, TN, USA, 8.Massachusetts General Hospital, Boston, MA, USA, 9.Biogen, Maidenhead, Berkshire, UK, 10.Biogen, Cambridge, MA, USA)