[Pe-034] Myopathy (DMD/BMD1)

[Pe-034-1] Exon 45 skipping therapy of iPS cells from a DMD patient with exon 46-55 deletion

^○Mitsuto Sato¹, Daigo Miyazaki^1,2, Yuji Shiba³, Yusuke Echigoya⁴, Toshifumi Yokota⁴, Yoshitsugu Aoki⁵, Shinichi Takeda⁵, Akinori Nakamura¹ (1.Department of Medicine (Neurology and Rheumatology) Shinshu University School of Medicine, 2.Intractable Disease Care Center, Shinshu University Hospital, 3.Institute for Biomedical Sciences, Shinshu University, 4.Department of Medical Genetics, School of Human Development, Faculty of Medicine and Dentistry, University of Alberta, 5.Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry (NCNP))