[Pe-33] English Poster Session 33 SBMA・others (basic research)

[Pe-33-2] Allele selective suppression of mutant polyQ protein by LNP-delivered siRNA targeting CAG expansions

^○Tomoki Hirunagi¹, Kentaro Sahashi¹, Kiyoshi Tachikawa², Angel Leu², Michelle Nguyen², Rajesh Mukthavaram², Priya Karmali², Padmanabh Chivukula², Genki Tohnai¹, Madoka Iida¹, Kazunari Onodera^1,3, Manabu Ohyama⁴, Yohei Okada³, Hideyuki Okano⁵, Masahisa Katsuno¹ (1.Department of Neurology, Nagoya University Graduate School of Medicine, Japan, 2.Arcturus Therapeutics, 3.Department of Neurology, Aichi Medical University School of Medicine, 4.Department of Dermatology, Keio University School of Medicine, 5.Department of Physiology, Keio University School of Medicine)