^○Harumasa Nakamura (Department of Clinical Research Support Clinical Research & Education Promotion Division, National Center Hospital National Center of Neurology and Psychiatry, Japan)

^○Madoka Mori-Yoshimura¹, Wakako Yoshioka², Yuji Takahashi¹, Ichizo Nishino^2,3, Harumasa Nakamura^4,5 (1.Department of Neurology, National Center Hospital, National Center of Neurology and Psychietry, Japan, 2.Department of Neuromuscular Research, National Institute of Neuroscience, National Center of Neurology and Psychiatry, 3.Medical Genome Center, National Center of Neurology and Psychiatry, 4.Clinical Research Support Office, Translational Medical Center Chief of Clinical Research/Trial Promotion Section, Translational Medical Center, National Center of Neurology and Psychiatry, 5.Clinical Research/Trial Promotion Section, Department of Clinical Research Promotion, National Center Hospital, National Center of Neurology and Psychietry)

^○Kentaro Sahashi¹, Masahisa Katsuno² (1.Department of Neurology, Nagoya University Hospital, Japan, 2.Department of Neurology, Nagoya University Graduate School of Medicine)

^○Kazuto Kato¹, Masanori P Takahashi², Tomoya Kubota², Beverley Anne Yamamoto³, Atsushi Kogetsu¹, Moeko Isono¹, Tatsuki Aikyo¹ (1.Department of Biomedical Ethics and Public Policy, Graduate School of Medicine, Osaka University, Japan, 2.Department of Clinical Laboratory and Biomedical Sciences, Division of Health Sciences, Graduate School of Medicine, Osaka University, 3.Graduate School of Human Sciences, Osaka University)

^○Straub Volker¹, Porter Ben², Walker Helen², TGDOC Subgroup Leads and Patient Representatives⁵, Guglieri Michela¹, Campbell Craig³, Ambrosini Anna⁴ (1.John Walton Muscular Dystrophy Research Centre, Newcastle University, UK, 2.TREAT-NMD Services Ltd., 3.Department of Paediatrics, Western University, 4.Fondazione Telethon, 5.Global TREAT-NMD Alliance)