[AO-01] Oral Presentation Award Nominee Session (Basic Research)

[AO-01-3] CDP-ribitol prodrug treatment ameliorates ISPD-deficient muscular dystrophy

^○Hideki Tokuoka^1,2, Rieko Imae³, Hitomi Nakashima², Hiroshi Manya³, Chiaki Masuda⁴, Shunsuke Hoshino³, Kazuhiro Kobayashi², Lefeber Dirk⁵, Riki Matsumoto¹, Takashi Okada⁶, Tamao Endo³, Motoi Kanagawa^2,7, Tatsushi Toda⁸ (1.Division of Neurology, Kobe University Graduate School of Medicine, Japan, 2.Division of Molecular Brain Science, Kobe University Graduate School of Medicine, Japan, 3.Molecular Glycobiology, Research Team for Mechanism of Aging, Tokyo Metropolitan Geriatric Hospital and Institute of Gerontology, 4.Department of Biochemistry and Molecular Biology, Nippon Medical School, 5.Department of Neurology, Radboud University Medical Center, 6.Division of Molecular and Medical Genetics, Center for Gene and Cell Therapy, The Institute of Medical Science, The University of Tokyo, 7.Department of Cell Biology and Molecular Medicine, Ehime University Graduate School of Medicine, 8.Department of Neurology, Graduate School of Medicine, The University of Tokyo)