[E1] English Session 1
Metabolic disease/Gene therapy

[E-004] A skeletal muscle model of infantile—onset Pompe disease using patient—specific iPS cells

Takeshi Yoshida^{1, 2}, Tomonari Awaya³, Tatsuya Jonouchi², Ryo Kimura³, Shigemi Kimura⁴, Kanako Maizuru¹, Masatoshi Nakata^{1, 3}, Atsushi Yokoyama¹, Takumi Era⁵, Hidetoshi Sakurai², Toshio Heike^{1, 6} (Department of pediatrics, Kyoto University Hospital, Kyoto, Japan¹, Center for iPS Cell Research and Application（CiRA）, Kyoto University, Kyoto, Japan², Department of Anatomy and Developmental Biology, Graduate School of Medicine, Kyoto University, Kyoto, Japan³, Kumamoto City Child Development Support Center, Kumamoto, Japan⁴, Department of Cell Modulation, Institute of Molecular Embryology and Genetics（IMEG）, Kumamoto University, Kumamoto, Japan⁵, Department of Pediatrics, Hyogo Prefectural Amagasaki General Medical Center, Hyogo, Japan⁶)