The 60th Annual Meeting of the Japanese Society of Child Neurology

Presentation information

イブニングセミナー

[ES] Evening Seminar
AVXS‒101 single‒dose gene‒replacement therapy for spinal muscular atrophy

Thu. May 31, 2018 6:30 PM - 7:20 PM Room 2 (International Conference Room)

Chair:Kayoko Saito(Institute of Medical Genetics, Tokyo Women’s Medical University)

共催:AveXis, Inc.

[ES-1] AVXS‒101 single‒dose gene‒replacement therapy for spinal muscular atrophy

Douglas M. Sproule1、Jerry R. Mendell2、3、4、Samiah Al-Zaidy2、3、Richard Shell3、W. Dave Arnold4、Louise Rodino-Klapac2、4、Thomas W. Prior5、Linda Lowes2、3、Lindsay Alfano2、3、Katherine Berry2、3、Kathleen Church2、3、John T. Kissel3、Sukumar Nagendran1、James L'Italien1、Courtney Wells1、Arthur H.M. Burghes4、6、Kevin D. Foust1、Kathrin Meyer2、Shibi Likhite2、Brian K. Kaspar2、3、4、1 (AveXis, Inc., Bannockburn, IL, USA1、Center for Gene Therapy Nationwide Children's Hospital, Columbus, OH, USA2、Department of Pediatrics, Ohio State University, Columbus, OH, USA3、Department of Neurology, Ohio State University, Columbus, OH, USA4、Department of Pathology, Ohio State University, Columbus, OH, USA5、Department of Molecular and Cellular Biochemistry, Ohio State University, Columbus, OH, USA6)

Abstract password authentication.
Password is required to view the abstract. Please enter a password to authenticate.

Password