[3P-739] AAV5 gene therapy for efficient treatment of lysosomal neuraminidase 1 deficiencies

^○Mizuki Miyoshi¹, Jun Tsukimoto¹, Yuto Horii¹, Yoshie Takeuchi², Nijiho Kamori², Rin Fukuike¹, Michiko Kino³, Naozumi Ishimaru³, Kohji Itoh^1,2 (1.Dept. of Medicin. Biotechnol.,Grad. Sch. of Pharmceut. Sci., Tokushima Univ., 2.Dept. of Medicin. Biotechnol., Fac. of Pharmceut. Sci., Tokushima Univ., 3.Dept. of Oral. Mol. Path., Grad. Sch. of Oral Sci., Tokushima Univ.)