[3SP-29-12] CDP-ribitol prodrug treatment ameliorates ISPD-deficient muscular dystrophy mouse model

^○Hideki Tokuoka¹, Rieko Imae², Hitomi Nakashima¹, Hiroshi Manya², Chiaki Masuda³, Shunsuke Hoshino², Kazuhiro Kobayashi¹, Dirk Lefeber⁴, Riki Matsumoto¹, Takashi Okada⁵, Tamao Endo², Motoi Kanagawa^6,1, Tatsushi Toda⁷ (1.Div. of Mol. Bra. Sci. and Neurol., Grad. Sch. of Med., Kobe Univ., 2.Mol. Glycobiol., Tokyo Metro. Inst. of Gerontol., 3.Dept. of Biochem. and Mol. Biol., Nippon Med. Sch., 4.Dept. of Neurol., Radboud Univ., 5.Div. of Mol. and Med. Genet., Inst. of Med. Sci., Univ. of Tokyo, 6.Dept. of Cell Biol. and Mol. Med., Grad. Sch. of Med., Ehime Univ., 7.Dept. of Neurol., Grad. Sch. of Med., Univ. of Tokyo)