[29P-am] 臨床生化学/病態モデル/疾病と遺伝子・遺伝子治療/薬理活性

[29P-am489] Pervasive Rescue of Pathogenesis in Globoid Cell Leukodystrophy by AAV-mediated Gene Therapy

○Dar-Shong Lin^1,2,3, Tsung-Han Lee³, Zo-Darr Huang³ (1. Dept of Pediatr, MacKay Memorial Hospital, Taipei, Taiwan, 2. Dept of Med. MacKay Med. College, New Taipei, Taiwan, 3. Dept of Med. Res., MacKay Memorial Hospital, Taipei, Taiwan)